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| DOI:doi:10.13407/j.cnki.jpp.1672-108X.2026.10.017 |
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| 基金项目:厦门市医疗卫生指导性项目,编号3502Z20244ZD1281。 |
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| Innovative Clinical Trial Design Strategies and Regulatory System for Pediatric Rare Disease Drugs inInternational Contexts |
| Chen Jinhua, Wu Xiuping |
| ((Xiamen Children’s Hospital, Xiamen Branch of Children’s Hospital of Fudan University, Fujian Xiamen
361006, China)) |
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